The objective of this paper is to address different aspects of the current management of DMD in the MENA region

MG is a chronic autoimmune neuromuscular disease characterized by varying degrees of weakness of the skeletal (voluntary) muscles.

SMA is an autosomal recessive neuromuscular disease affecting part of the nervous system that controls voluntary muscle movement.

Facioscapulohumeral Muscular Dystrophy is an inherited disorder of muscle that causes progressive deterioration of muscle fibers.

ALS is a progressive neurodegenerative disease that attacks nerve cells responsible for controlling voluntary muscles.

Progress in scientific and clinical research has paved the way to the first Gene Therapy drugs for rare and genetic diseases.